Dr. Patti Peeples, HealthEconomics.Com founder and CEO, recently discussed with HealthCore-NERI’s Flora Siami on the evolving clinical trial landscape for orphan and rare diseases using real-world evidence.
Siami says there are a number of key challenges involved with developing and testing therapies for rare and orphan diseases.
“Because there are a limited number of people with the disease/condition, physicians may not be aware of the most appropriate way to diagnose the condition,” she said. “Even if the disease/condition is diagnosed, there may be limited clinical information available to understand the disease/condition outside of published case studies.”
The mission of HealthCore-NERI is to provide clarity that empowers decision makers to act with precision to improve quality, safety, and affordability in healthcare.
To read the full discussion on HealthEconomics.Com’s official blog, tHEORetically Speaking, click here.
